August 7, 2021 Antenatal and perinatal factors influencing neonatal blood pressure: a systematic review
August 1, 2021 A Disease Progression Model to Quantify the Nonmotor Symptoms of Parkinson’s Disease in Participants With Leucine-Rich Repeat Kinase 2 Mutation Ahamadi M, Mehrotra N, Hanan N, Lai Yee K, Gheyas F, Anton J, Bani M, Boroojerdi B, Smit H, Weidemann J, Macha S, Thuillier V...
July 21, 2021 View Now | How RDCA-DAP Can Help Inform Optimal Trial Design in Progressive Rare Disease When: July 21, 2021, 12 p.m. ET Case Study: Northstar Ambulatory Assessment as an outcome assessment in Duchenne muscular
July 16, 2021 View Now | RDCA-DAP Webinar Series: Value of Integrated Data and Analytics in Rare Disease Drug Development When: June 16, 2021, 12 p.m. ET Case Study: Modeling disease progression in polycystic kidney disease to inform tr
July 15, 2021-July 26, 2021 VIEW NOW | Design of Clinical Trials in New-Onset Type 1 Diabetes: Regulatory Considerations for Drug Development Critical Path Institute held a free virtual workshop, Design of Clinical Trials in New-Onset Type 1 Diabetes: Regulatory Cons
July 8, 2021 Digital Progression Biomarkers as Novel Endpoints in Clinical Trials: A Multistakeholder Perspective Stephenson D, Badawy R, Mathur S, Tome M, Rochester L. Digital Progression Biomarkers as Novel Endpoints in Clinical Trials...
June 27, 2021-July 1, 2021 The Rare Disease Clinical Outcome Assessment Consortium: Collaboration Aimed at Accelerating Rare Disease Drug Development Presented at the DIA Virtual Global Annual Meeting, held June 27 – July 1, 2021.
May 20, 2021 The Role of Patient-reported Outcomes and Medication Adherence Assessment in Patient-focused Drug Development for Solid Organ Transplantation
May 19, 2021-May 20, 2021 View Now | 2021 PKD Regulatory Summit | May 19-20 The Critical Path Institute’s Polycystic Kidney Disease Outcomes Consortium (PKDOC), The PKD Foundation and Otsuka invite you vi
May 19, 2021 View Now | Interpretation of novel biomarkers in related diseases through data interoperability in a pan-rare disease database When: May 19, 2021, 12 p.m. ET Example Disease: Polycystic kidney disease and kidney transplant Presenters: Jagde
